Orphan Now is a consulting organization that guides and supports orphan drug companies in their quest of developing and commercializing needed therapies for patients with rare diseases

Our advisory and consulting services focus on helping orphan drug companies at:

  • Putting patients at the center of everything they do
  • Designing clinical programs that leave no patients behind
  • Obtaining swift and broad marketing authorizations with the potential to transform the lives of patients with rare diseases
  • Creating the conditions required for patients to have fast and sustainable access to the medicines they need
  • Driving educational and commercial efforts to maximize patient benefits
  • Delivering the promise of their needed therapies to patients globally

At Orphan Now, we turn NO into NOW for rare disease patients and orphan drug companies. ®